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Sarcoidosis

Sarcoidosis is a multisystem inflammatory disease of unknown etiology that predominantly affects the lungs and intrathoracic lymph nodes

Prevalence

1–2 / 10,000

33,100–66,200

US Estimated

51,350–102,700

Europe Estimated

Age of Onset

Adults

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ICD-10

D86.9

Inheritance

Autosomal dominant

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Autosomal recessive

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Mitochondrial/Multigenic

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X-linked dominant

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X-linked recessive

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5 Facts you should know

FACT

1

It is most often defined by the presence of noncaseating granulomatous inflammation that occurs in the absence of infection, exposures, malignancy, or alternative immune-related disease

 

FACT

2

Lung and thoracic lymph nodes are most often involved, but any organ can be affected

 

FACT

3

Patients with multi-system involvement have a worse prognosis

FACT

4

The basis of treatment of sarcoidosis is regulation of the heightened immune response and suppression of granulomatous inflammation in order to prevent dangerous interference with organ function

 

FACT

5

Use of corticosteroids and other immunomodulatory agents is often modeled on how they are used in other autoimmune and inflammatory diseases in which suppression of the immune system is desired

 

Sarcoidosis is also known as...

Sarcoidosis is also known as:

  • Besnier–Boeck–Schaumann disease

What’s your Rare IQ?

Which famous NBA “big man” was diagnosed with sarcoidosis?

Common signs & symptoms

Persistent dry cough

Eye or skin manifestations

Peripheral lymph nodes

Fatigue

Weight loss

Fever

Night sweats

Löfgren syndrome.

Current treatments

Treatment depends on disease severity and organ involvement.

Observation (mild, asymptomatic cases)

Corticosteroids (first-line therapy)

Immunosuppressive agents:

  • Methotrexate
  • Azathioprine

Biologic therapies (e.g., TNF inhibitors in refractory cases)

Clinical trials

TitleDescriptionPhasesStatusInterventionsMore Information
Efficacy and Safety Study of OATD-01 in Patients With Active Pulmonary SarcoidosisThis is a Phase 2, randomized, double-blind, placebo-controlled, adaptive, multicenter study to evaluate the efficacy, safety, tolerability, Pharmacodynamics (PD), and Pharmacokinetics (PK) of OATD-01 in the treatment of subjects with active pulmonary sarcoidosis.Phase 2RecruitingDrug: OATD-01
Drug: Placebo
More Info
Cardiac Sarcoidosis Randomized TrialProspective randomized controlled trial comparing low dose Prednisone(or Prednisolone)/Methotrexate combination to standard dose Prednisone(or Prednisolone) in patients diagnosed with acute active clinically manifest cardiac sarcoidosis and not yet treated.

The Investigators hypothesize that low do...
Phase 3RecruitingDrug: Prednisone or Prednisolone
Drug: Methotrexate
More Info
Evaluation of TNF-alpha Antagonists (Infliximab) Withdrawal in SarcoidosisIn severe refractory sarcoidosis not responding to conventional immunosuppressive treatment, the third-line tumor necrosis factor (TNF)-alpha inhibitor infliximab is an alternative. Treatment duration is not known, although it has been suggested that relapse rates after withdrawal could be high. We...Phase 3ActiveDrug: STOP armMore Info
A Phase 2 Study of the Safety and Efficacy of Brepocitinib in Adults With Cutaneous Sarcoidosis (BEACON)This study will evaluate the clinical safety and efficacy of oral brepocitinib in participants with cutaneous sarcoidosis.Phase 2RecruitingDrug: Oral Brepocitinib
Drug: Oral Placebo
More Info
RCT of Nintedanib in Fibrotic SarcoidosisSarcoidosis is generally managed with outdoor immune modulatory drugs, most commonly oral steroids and at times drugs like methotrexate or azathioprine as a steroid sparing agent.

Around 15-20% of sarcoidosis patient develop fibrosis of the lung parenchyma. The effect of antifibrotics in such patie...
Phase 4RecruitingDrug: Nintedanib
Drug: Standard of care
More Info
Prednisolone for 12 Versus 6 Months to Treat Pulmonary SarcoidosisIn this study, the efficacy and safety of treating pulmonary sarcoidosis with 12 months vs. 6 months of prednisolone will be compared. The hypothesis is that longer treatment DURAtion would be more effective in preventing treatment failure or early relapse in SARCoidosis (DURASARC trial). The premis...Phase 4Not yet recruitingDrug: PrednisoloneMore Info
Effectiveness of Methotrexate Versus Prednisone as First-line Therapy for Pulmonary SarcoidosisThis is a prospective, randomized, non-blinded, multi-center, non-inferiority trial designed to compare effectiveness and side-effects of methotrexate versus prednisone as first-line therapy for pulmonary sarcoidosis.Phase 4ActiveDrug: Methotrexate
Drug: Prednisone
More Info
Diagnostic Criteria in Cardiac SarcoidosisThe purpose of the study is to evaluate the accuracy of the current diagnostic criteria of cardiac sarcoidosis.RecruitingDiagnostic_Test: ECG, Echo, laboratory tests, CMR, PET-CT, BiopsyMore Info
Evaluation of the Prognostic Value of PET/MRI in Cardiac SarcoidosisCardiac damage is the second leading cause of death in patients with sarcoidosis, after lung damage. Today's challenge is to diagnose the disease as effectively as possible, and to develop tools for better risk stratification, especially for sudden death, in order to better target therapies and impl...RecruitingDiagnostic_Test: PET/MRIMore Info
Comparing Menghini-type Needle and Franseen-type Needle in EBUS-TBNA for SarcoidosisThis randomized pilot clinical trial aims to examine whether sample collection with Franseen-type needles are effective for the diagnosis of sarcoidosis, as defined by improved sample quality for pathological diagnosis compared to the conventional Menghini-type needle.RecruitingDevice: endobronchial ultrasound-guided transbronchial needle aspiration (EBUS-TBNA)More Info

References:

Iannuzzi MC, Rybicki BA, Teirstein AS. Sarcoidosis. N Engl J Med. 2007;357(21):2153–2165. doi:10.1056/NEJMra071714Valeyre D, Prasse A, Nunes H, et al. Sarcoidosis. Lancet. 2014;383(9923):1155–1167. doi:10.1016/S0140-6736(13)60680-7Baughman RP, Culver DA, Judson MA. A concise review of pulmonary sarcoidosis. Am J Respir Crit Care Med. 2011;183(5):573–581. doi:10.1164/rccm.201006-0865CIStatement on Sarcoidosis. American Thoracic Society (ATS). Am J Respir Crit Care Med. 1999;160(2):736–755.